Search Results 11-20 of 15968 for Duchenne+muscular+dystrophy
About this study. The expanded access program will provide access to treatment with deflazacort in children, adolescent, and adult patients with DMD in the ...
The expanded access program will provide access to treatment with deflazacort in children, adolescent, and adult patients with DMD in the U.S. who are ...
Casimersen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle ...
Viltolarsen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle ...
Nine people around the world who have been living with unexplained, muscular dystrophy-like symptoms may now have an answer.
Researchers reviewed all of the available studies on the muscular dystrophy, a group of genetic diseases in which muscle fibers are unusually susceptible to ...
Gene therapy for muscular dystrophies requires that most, if not all, muscle fibers receive the appropriate gene to correct the underlying genetic defect.
... muscular atrophy, hemophilia and sickle cell disease. ... This gene therapy is for children ages 4 through 5 years who have Duchenne muscular dystrophy and a ...
... muscles due to problems with the nerves and muscles in your body. ... Lambert-Eaton syndrome; Mitochondrial myopathy; Motor neuron disease; Muscular dystrophy ...
Duchenne muscular dystrophy; Facioscapulohumeral muscular dystrophy; Juvenile amyotrophic lateral sclerosis; Juvenile dermatomyositis; Juvenile motor neuron ...
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