Resultados de la búsqueda 31-40 of 9459 for Pompe Disease
The purpose of this study is to identify clinical characteristics and biomarkers predictive of disease outcome, progression, and treatment response in ...
... diseases. A "Registry" is a list of basic information about people who have a certain disease or condition in common. These immune deficiency diseases are ...
Congenital heart disease (CHD) is an abnormal formation that occurs during the development of a baby's heart, heart valves and/or large vessels such as the ...
Genetic Disease Foundation (Fundación de Enfermedades Genéticas). http://www.geneticdiseasefoundation.org/genetic-diseases/gaucher-disease-type-i/. Último ...
Accessed June 7, 2023. Wilson disease. National Institute of Diabetes and Digestive and Kidney Diseases. https://www.niddk.nih.gov/health-information/liver- ...
The purpose of this study is to evaluate whether or not semaglutide can slow down the growth and worsening of chronic kidney disease in people with type 2 ...
... disease (CKD), primary hyperoxaluria (PH), cystinuria, Dent disease and ... Cross-comparisons among the disorders will allow us to better evaluate mechanisms of ...
Study of Breast Cancer Risk Assessment in Female Patients with Benign Breast Disease. Rochester, Minn., Jacksonville, Fla. The purpose of this study is to to ...
The aim of this study is to examine the role of mast cell mediators in children with allergic disorders in a two part study.
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