Search Results 1-10 of 15787 for Duchenne+muscular+dystrophy

  1. Mayo Clinic Q and A: Understanding Duchenne muscular dystrophy

    Currently, there is no cure. Muscular dystrophy is an umbrella term applied to a group of muscle diseases in which there is a known genetic abnormality that ...

  2. Muscular dystrophy - Symptoms & causes - Mayo Clinic

    Muscle pain and stiffness; Learning disabilities; Delayed growth. Becker muscular dystrophy. Signs and symptoms are similar to those of Duchenne muscular ...

  3. Muscular dystrophy - Diagnosis & treatment - Mayo Clinic

    In 2019, the Food and Drug Administration (FDA) approved golodirsen (Vyondys 53) for treatment of some people with Duchenne dystrophy who have a certain genetic ...

  4. Deflazacort (Oral Route) Description and Brand Names - Mayo Clinic

    Deflazacort is used to treat Duchenne muscular dystrophy (DMD). DMD is a rare, inherited muscle disease that occurs usually in children and young adults and ...

  5. Viltolarsen (Intravenous Route) Description and Brand Names - Mayo Clinic

    Viltolarsen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle ...

  6. Givinostat (Oral Route) Description and Brand Names - Mayo Clinic

    Givinostat is used to treat Duchenne muscular dystrophy (DMD). DMD is a rare, inherited muscle disease that is caused by the absence of a protein called ...

  7. Delandistrogene Moxeparvovec-Rokl (Intravenous Route) Description and Brand Names - Mayo Clinic

    ... Duchenne muscular dystrophy (DMD) in patients with a confirmed specific genetic mutation. DMD is a rare, inherited muscle disease that is caused by absence ...

  8. Vamorolone (Oral Route) Description and Brand Names - Mayo Clinic

    Vamorolone is used to treat Duchenne muscular dystrophy (DMD). DMD is a rare, inherited muscle disease that is caused by absence of a protein called ...

  9. Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy - Mayo Clinic

    About this study. The expanded access program will provide access to treatment with deflazacort in children, adolescent, and adult patients with DMD in the ...

  10. Eteplirsen (Intravenous Route) Description and Brand Names - Mayo Clinic

    Eteplirsen injection is used to treat Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation of the dystrophin gene amenable to exon 51 ...